There is no cure, and the disease considerably shortens life expectancy. Friedreich’s ataxia is an inherited disease that affects the nervous system, especially the spinal cord, peripheral ...
Treatment success was measured as a change from baseline in the modified Friedreich’s Ataxia Rating Scale (mFARS) score. The mFARS is an assessment of neurological function and tests ...
During the segment, she highlighted the upcoming “On the Move to Cure Ataxia” 5K event, aiming to raise awareness and funds for Ataxia research and support through the National Ataxia Foundation.
Repare Therapeutics said it received encouraging early phase 1 data for its camonsertib inhibitor combined with palliative radiation for the treatment of metastatic tumors harboring an ...