Fanconi anemia (FA) is a rare genetic disease, affecting 1 in 160,000 people. The condition leads to gradual bone marrow failure in about 90% of people affected. Bone marrow is the spongy material ...

Although rare, Fanconi anaemia is the most common form of inherited bone marrow failure that requires bone marrow transplantation therapy in Saudi Arabia. Paediatrician Abdulrahman Alsultan and ...

Their hunt narrowed to a set of genes involved in the Fanconi anemia pathway—a DNA repair mechanism mutated in an eponymous germline condition marked by severe anemia, bone marrow failure ...

"I feel like I just blacked out," donor Maycie Fuselier said of the emotional moment she met 8-year-old Sophie Cromer WVTM 13 News An 8-year-old girl from Alabama had a tearful meeting with the ...

The main causes of acquired anemia can be divided into loss of blood (hemolysis or hemorrhage) or inadequate bone-marrow function ... role of underlying chronic disease such as cirrhosis or ...

Bone marrow transplant for aplastic anemia Aplastic anemia is a rare disease that causes your bone marrow to stop producing blood cells, making it a very serious illness. A blood transfusion can ...

The community unites to host a music festival to fundraise for Dylan René, 6, and her father, Josiah Menard who are facing ...

Bone Marrow Transplantation (BMT) offers hope for rare blood disorders like leukaemia, thalassemia, and aplastic anaemia by replacing defective bone marrow with healthy stem cells. Though challenges ...

What are the Common Causes of Anemia in CHF ... reduced activity of EPO in the bone marrow, hepcidin-induced failure of iron absorption from the gut, and hepcidin-induced trapping of iron in ...

Its clinical program is an LVV-based gene therapy for the treatment of Fanconi Anemia (FA), a difficult to treat genetic disease that leads to bone marrow failure and potentially cancer.

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable ...

New Delhi: The Central government is set to launch a scheme to develop 12 indigenous drugs for eight rare diseases, health ...