Larimar Therapeutics' CTI-1601 offers hope for Friedreich's ataxia patients, with promising trial results. Check out why LRMR ...
Friedreich’s ataxia is a progressive neuromuscular disease that causes uncoordinated movement, muscle weakness, balance problems, impaired speech, and frequently, heart abnormalities.
Most people haven’t heard of the condition, but Friedreich’s ataxia is getting more attention because of a new treatment and ...
Panelists discuss how the differential diagnosis for Friedreich's Ataxia involves distinguishing it from other ataxias, the ...
Treatment success was measured as a change from baseline in the modified Friedreich’s Ataxia Rating Scale (mFARS) score. The mFARS is an assessment of neurological function and tests ...
Bill Nye, the beloved 'Science Guy' says many of his family members suffer from Ataxia, a rare neurological disorder that ...
DeBoer welcomed 10-year-old Susanna to the team. Susanna is battling Friedreich's Ataxia, which usually attacks the nervous system and, in her case, is also eating up her heart. But Susanna is a ...
After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.
In your opinion, what are the most promising emerging therapeutic avenues for managing advanced stages of FA, and how do you see them impacting clinical practice in the future?
Larimar will present three posters during the conference, one of which will also be presented as an oral presentation. The poster presentations are as follows: Effect of nomlabofusp administration on ...
Krystie Maddox, 12, who lives in Wolverhampton with her mother Molvia, 40, a business consultant and stepfather Mitchell, 34, also a consultant, has Friedreich's Ataxia, a rare inherited disorder ...