The city's first guide to quality management of cell therapy drugs used in medical institutions was released on Tuesday, ...

The U.S. Food and Drug Administration approved PTC Therapeutics' gene therapy to treat a potential fatal enzyme deficiency ...

A 29-year-old local patient is about to undergo a life-changing treatment that could dramatically alter the course of his ...

Most discussion of gene and cell therapy costs focuses on increasing manufacturing efficiency but reducing costs can only go ...

Modifying Treatment for AADC Deficiency in the United States SOLANA BEACH, CA / ACCESSWIRE / November 13, 2024 / ...

Bayer has become the latest in a long line of drug developers to give up on Huntington’s disease after the German pharma ...

An RNA-editing gene therapy has been developed that switches off the key driver of common eye conditions affecting diabetics ...

Michael Okunewitch, an analyst from Maxim Group, maintained the Buy rating on Ocugen (OCGN – Research Report). The associated price ...

Join the GenScript Biotech Global Forum in London to Navigate the Future of Cell and Gene Therapies. For more information, ...

Neurogene has reported encouraging efficacy results with its gene therapy for rare genetic disorder Rett syndrome, but ...

University of Wisconsin-Madison researchers targeting a group of hereditary neurodegenerative diseases have found success ...

WARREN, N.J., Nov. 13, 2024 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) announced today the U.S. Food and Drug Administration (FDA) accelerated approval of its gene therapy for the treatment ...