Liver-specific SMN1 gene therapy both improved liver functioning, and also reduced other SMA-like symptoms in a mouse model ...

Columnist Alyssa Silva had an epiphany on a recent trip to Boston: She can battle her discouraging days by finding gratitude.

Recent progress in SMA research and advocacy was celebrated at Cure SMA's annual Hope on the Hill event in Washington, D.C.

Individually and collectively, it’s vital to be sensitive to what’s happening in the world around us. This awareness allows us to be empathetic and strive for change that improves society for ...

More than half of SMA patients in an Australian survey said they did not notice any improvement in their symptoms following ...

Muscle fibers in children with SMA type 1 show substantial differences in components of the myosin protein called heavy ...

Columnist Kevin Schaefer feels adulthood with SMA is like a "Star Trek" mission: to boldly go into uncharted territory.

Since her SMA assignment, columnist Helen Baldwin has learned to look for the bright spots — even in Hurricane Helene's ...