Tiffany Young On August 7, actor Colin Farrell opened up about his son James' life with Angelman syndrome, a rare neurogenetic disorder that affects about 500,000 people worldwide. According to ...
Shortly after his first birthday, we received the diagnosis that would change our lives forever: Theodore tested positive for a rare neurogenetic disorder called Angelman syndrome. AS is a random ...
Ionis has committed to a phase 3 programme for its antisense therapy for rare genetic disorder Angelman syndrome, just weeks after Biogen decided against exercising an option to license the drug.