No writing assistance was utilized in the production of this manuscript. Vulvovaginal atrophy, which can have a large impact on quality of life and sexual function, is often underdiagnosed and ...

利司扑兰是由瑞士罗氏制药公司开发的运动神经元生存基因2（SMN2）剪接修饰剂，于2020年8月在美国获批，2021年6月在中国获批，是首个被批准用于SMA的口服治疗药物，作为全球首个获批的直接以RNA为靶点发挥作用的小分子药物，其作用机制是通过靶向屏 ...

A large, retrospective analysis of patients with amyotrophic lateral sclerosis (ALS) and progressive muscular atrophy (PMA) indicates that a substantial proportion of PMA patients develop upper ...

The brain naturally begins to atrophy beginning in one’s 30s and 40s. But this can become much more pronounced with dementia ...

Public health groups are challenging Roche's attempt to block a generic version of its expensive Spinal Muscular Atrophy drug ...

You can still live a full life with geographic atrophy (GA). Even though your vision may be different, GA doesn’t lead to total blindness. You can use your remaining vision and make certain ...

A rare spinal surgery in Thiruvananthapuram, India, has transformed the life of 23-year-old Mohamad Raishan Ahmed from the ...

Astellas Pharma Inc. has withdrawn its marketing authorization application from the EMA for its avacincaptad pegol intravitreal solution for the treatment of geographic atrophy secondary to ...

Despite diagnostic and therapeutic advances, mortality and the multi-systemic health impact of SMA continue to be experienced ...