What makes it special is the fact the therapy targets RNA, instead of DNA. So, what does that mean, and why should we be excited? Genes are made up of DNA, or deoxyribonucleic acid. Nearly all ...
What makes it special is the fact the therapy targets RNA, instead of DNA. So, what does that mean, and why should we be excited? What is gene editing and how is it used? Genes are made up of DNA ...
The researchers considered developing a gene therapy as an effective alternative to these regular eye injections. For the first time, they used the RNA editing tool CRISPR-Cas13 to suppress the ...
StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.