Karnataka launched free treatment for Spinal Muscular Atrophy (SMA) at the Indira Gandhi Institute of Child Health in ...

CPCT provides free lifelong access to Risdiplam for 50 children with SMA, supported by Roche Pharma India and Karnataka government.

Alpana Sharma, founder-director of CureSMA, a parent-led advocacy group, urges the government to include medicines for SMA in ...

Download this article from The Scientist’s Creative Services Team and Revvity to discover how dry PCR enables more effective ...

Medicine is on the precipice of radical changes in diagnosis, personalised treatment, and the ability to prevent disease ...

Moreover, Biohaven’s Phase 3 trial of taldefgrobep alfa in SMA is expected to gain attention following positive results from a ... therapies to improve the lives of patients with debilitating ...

Analyst Marc Goodman from Leerink Partners maintained a Buy rating on Biohaven Ltd. (BHVN – Research Report) and keeping the price target ...

REGENXBIO is advancing a pipeline of AAV Therapeutics for rare and retinal diseases, including RGX-202 for the treatment of Duchenne ... including Novartis' Zolgensma ® for children with spinal ...

Please note that on today's call, we will be making forward-looking statements, including statements concerning the potential of TSHA-102, including the reproducibility and durability of any favorable ...

Margao: Families caring for children with chronic illnesses and neurological disorders require a respite centre in Goa where they can temporarily leav.