PJ Snyder has difficulty walking on his own, but will compete in the Chicago Marathon with help from a friend and volunteer ...

Farrell, star of "The Penguin," is a father of two children. When he's not in the limelight, Colin Farrell is a proud father ...

Tiffany Young On August 7, actor Colin Farrell opened up about his son James' life with Angelman syndrome, a rare neurogenetic disorder that affects about 500,000 people worldwide. According to ...

在该研究中，研究团队通过在天使综合征（AS）小鼠模型中引入这一表观遗传编辑系统，成功实现了 UBE3A ...

Shortly after his first birthday, we received the diagnosis that would change our lives forever: Theodore tested positive for a rare neurogenetic disorder called Angelman syndrome. AS is a random ...

Colin Farrell hit the red carpet with his rarely photographed teenage son this week at the New York premiere of his new TV ...

Cartwright and his wife Tammy lost their 28-year-old daughter, Haley Elizabeth Michele Cartwright, last Sunday from injuries ...

Ionis has committed to a phase 3 programme for its antisense therapy for rare genetic disorder Angelman syndrome, just weeks after Biogen decided against exercising an option to license the drug.