German drugmaker Boehringer Ingelheim has its first regulatory approval for spesolimab, its antibody therapy for rare and life-threatening ... treat other skin diseases, such as palmoplantar ...
Timber's lead candidate TMB-001 for rare skin disease congenital ichthyosis failed to meet its efficacy objectives across the board in the ASCEND trial and will not support a planned regulatory ...
Jason McCarthy’s rating is based on a combination of factors related to Azitra Inc’s recent progress and future potential in developing treatments for rare skin diseases. The company’s ...
has to completely cover her skin head to toe to avoid the searing ... according to the National Organization for Rare Disorders. Both of her parents carry a gene variant that causes the disease ...
PEOPLE spoke to Brandon Joseph, who is living with the rare disease epidermolysis bullosa. While many patients die during infancy, Joseph is now thriving at 20 ...